A hopeful therapy for Niemann-Pick C diseases - The Lancet
Por um escritor misterioso
Last updated 20 setembro 2024
A first therapy for Niemann-Pick C - The Lancet Neurology
Pharmaceuticals, Free Full-Text
Central nervous system therapy for lysosomal storage disorders in
Neurological manifestations of lysosomal disorders and emerging
Miglustat for treatment of Niemann-Pick C disease: a randomised
IJMS, Free Full-Text
PDF) Diagnostic workup and management of patients with suspected
Identification of Niemann-Pick C1 disease biomarkers through
Experimental treatment for Niemann-Pick disease type C1 appears
Intrathecal 2-hydroxypropyl-β-cyclodextrin decreases neurological
A hopeful therapy for Niemann-Pick C diseases,The Lancet - X-MOL
Understanding the phenotypic variability in Niemann-Pick disease
Lysosomal storage diseases: Diagnostic confirmation and management
Families plead with FDA for drug to treat Niemann-Pick Disease Type C
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