A hopeful therapy for Niemann-Pick C diseases - The Lancet

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Last updated 20 setembro 2024
A hopeful therapy for Niemann-Pick C diseases - The Lancet
A hopeful therapy for Niemann-Pick C diseases - The Lancet
A first therapy for Niemann-Pick C - The Lancet Neurology
A hopeful therapy for Niemann-Pick C diseases - The Lancet
Pharmaceuticals, Free Full-Text
A hopeful therapy for Niemann-Pick C diseases - The Lancet
Central nervous system therapy for lysosomal storage disorders in
A hopeful therapy for Niemann-Pick C diseases - The Lancet
Neurological manifestations of lysosomal disorders and emerging
A hopeful therapy for Niemann-Pick C diseases - The Lancet
Miglustat for treatment of Niemann-Pick C disease: a randomised
A hopeful therapy for Niemann-Pick C diseases - The Lancet
IJMS, Free Full-Text
A hopeful therapy for Niemann-Pick C diseases - The Lancet
PDF) Diagnostic workup and management of patients with suspected
A hopeful therapy for Niemann-Pick C diseases - The Lancet
Identification of Niemann-Pick C1 disease biomarkers through
A hopeful therapy for Niemann-Pick C diseases - The Lancet
Experimental treatment for Niemann-Pick disease type C1 appears
A hopeful therapy for Niemann-Pick C diseases - The Lancet
Intrathecal 2-hydroxypropyl-β-cyclodextrin decreases neurological
A hopeful therapy for Niemann-Pick C diseases - The Lancet
A hopeful therapy for Niemann-Pick C diseases,The Lancet - X-MOL
A hopeful therapy for Niemann-Pick C diseases - The Lancet
Understanding the phenotypic variability in Niemann-Pick disease
A hopeful therapy for Niemann-Pick C diseases - The Lancet
Lysosomal storage diseases: Diagnostic confirmation and management
A hopeful therapy for Niemann-Pick C diseases - The Lancet
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